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MACC Fund Center for Cancer and Blood Disorders
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- Active clinical trials for pediatric cancers
- CAR-20/19-T cells in pediatric and young adult patients with relapsed/refractory B Cell Acute Lymphoblastic Leukemia (CAR-20/19-T) phase 1 clinical trial
- Unrelated and partially matched related donor peripheral stem cell transplantation for patients with hematologic malignancies clinical trial
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Treosulfan for bone marrow transplant for nonmalignant diseases
Children’s Wisconsin is currently enrolling patients on a Phase II clinical trial of Treosulfan, which is used in combination with other chemotherapy drugs in patients with nonmalignant diseases treatable by allogeneic transplant, including:
Sickle cell disease- Thalassemia
- Bone marrow failure syndromes
- Diamond-blackfan anemia
- Shwachman-diamond
- Dyskeratosis congenita
- HLH
- Primary immunodeficiencies
- Osteopetrosis
Children’s is one of only two sites in the country where this trial is available. We are participating in collaboration with The Fred Hutchinson Cancer Research Center in Seattle.
Being picked to participate in this select study is evidence of our transplant program’s dedication and expertise. Our program is FACT (Foundation for the Accreditation of Cellular Therapy) accredited and has performed over 1,100 bone marrow transplants. Children’s also ranked in 9 specialty areas in the U.S. News & World Report Best Children’s Wisconsins list.
Contact us
For more information about cancer and blood disorders clinical trials, email us or call
(414) 955-4727
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It's important to know what your options are. We can provide expert opinions to verify or give more information about an initial diagnosis. Contact us today.
Why participate in clinical trials?
