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Treosulfan for bone marrow transplant for nonmalignant diseases
Children’s Wisconsin is currently enrolling patients on a Phase II clinical trial of Treosulfan, which is used in combination with other chemotherapy drugs in patients with nonmalignant diseases treatable by allogeneic transplant, including:
- Sickle cell disease
- Bone marrow failure syndromes
- Diamond-blackfan anemia
- Dyskeratosis congenita
- Primary immunodeficiencies
Children’s is one of only two sites in the country where this trial is available. We are participating in collaboration with The Fred Hutchinson Cancer Research Center in Seattle.
Being picked to participate in this select study is evidence of our transplant program’s dedication and expertise. Our program is FACT (Foundation for the Accreditation of Cellular Therapy) accredited and has performed over 1,100 bone marrow transplants. Children’s also ranked in 9 specialty areas in the U.S. News & World Report Best Children’s Wisconsins list.
For more information about cancer and blood disorders clinical trials, email us or call
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"The steady improvement in survival for children with cancer is a direct result of their enrollment onto clinical trials; without which we would remain decades behind in terms of scientific advances in pediatric cancer." ~Michael J. Burke, MD